Disease & care

Medical Glossary

A practical glossary for terms used on this site: meaning, where you might see them, when you might encounter them, with examples and links — not a diagnostic checklist.

Last reviewed: September 2026
How to read this page

Each term uses three columns:

  • Column 1: name, abbreviation if any, related-page link, and context badges (lab, genetics, and so on) only when they truly apply.
  • Column 2: What is it? Where might you see it? When might you encounter it? — practical wording for families and clinics.
  • Column 3: Where on this site? and a practical example that illustrates use without making the term mandatory for every patient.

This page is not a diagnostic checklist. Full scientific context and limits live on the disease, treatment, what-we-know, and sources pages.

“Where might you see it” does not mean “the clinician must order it.” Examples are illustrative only.

Carbonic Anhydrase II
CA II / CA2
Related page

Genetics Bone Kidney Research

What is it?

An enzyme that helps some tissues regulate acid–base balance. It is encoded by the CA2 gene.

Where might you see it?

In genetics reports, disease summaries, and papers discussing “CA II deficiency” or CA2-related disease.

When might you encounter it?

When explaining the diagnosis or comparing bone, kidney, and neurologic features linked to this condition.

Where on this site?

About the disease · Treatment · What we know

Practical example

A genetics report listing CA2 variants together with osteopetrosis and renal tubular acidosis may lead clinicians to describe carbonic anhydrase II deficiency — severity still varies between people.

Renal Tubular Acidosis
RTA
Related page

Kidney Lab Clinic Clinical reports

What is it?

A problem with how the kidneys manage blood acidity; it is not automatically the same as global kidney failure.

Where might you see it?

In nephrology diagnoses, follow-up summaries, and acid–base or electrolyte results.

When might you encounter it?

When discussing acidosis, bicarbonate, potassium, or individualized alkali support decided by the care team.

Where on this site?

Treatment — RTA · Glossary · Clinical quick reference · Family toolkit

Practical example

A note saying “mixed RTA” with low HCO3 does not by itself define one care plan for every patient; teams interpret the pattern in full clinical context.

Distal RTA
dRTA
Related page

Kidney Lab Clinical reports

What is it?

An RTA pattern mainly linked to impaired acidification in the distal nephron.

Where might you see it?

In nephrology reports or differential classification of RTA.

When might you encounter it?

When a clinician or report describes distal features within tubular acidosis.

Where on this site?

Treatment — RTA · RTA in the glossary

Practical example

“Distal RTA” names a physiologic pattern. In CA II deficiency, distal features may appear within a mixed picture and are not a fixed label for every case.

Proximal RTA
pRTA
Related page

Kidney Lab Clinical reports

What is it?

An RTA pattern linked to impaired bicarbonate reabsorption in the proximal tubule.

Where might you see it?

In kidney reports or discussions of urinary bicarbonate loss.

When might you encounter it?

When interpreting low HCO3 or alkali needs within RTA follow-up.

Where on this site?

Treatment — RTA · Bicarbonate

Practical example

Mention of “proximal bicarbonate wasting” can signal proximal features; it is a clinical/lab description, not a ready-made prescription.

Mixed RTA
Related page

Kidney Clinical reports Clinic

What is it?

Wording used when reports describe proximal and distal features together; common in published CA II deficiency cases.

Where might you see it?

In diagnostic summaries or case reports describing mixed tubular acidosis.

When might you encounter it?

When comparing patient reports or reading the treatment page on RTA in CA II.

Where on this site?

Treatment — RTA · What we know

Practical example

Many CA II reports use “mixed RTA”; that does not mean every patient shares the same label or the same follow-up plan.

pH
pH
Related page

Blood gas Lab Clinic

What is it?

A measure of how acidic or alkaline blood or body fluids are.

Where might you see it?

On blood gas results and some electrolyte/acid–base panels.

When might you encounter it?

During illness, acidosis follow-up, or clinic review of laboratory results.

Where on this site?

Family toolkit · Clinical quick reference · Treatment — RTA

Practical example

A low blood-gas pH may prompt the team to reassess acidosis and supportive care — the clinician decides timing; not every visit requires a blood gas.

Bicarbonate
HCO3
Related page

Blood gas Lab Kidney Treatment

What is it?

A key buffer that helps offset acidity; often reported on blood gas or chemistry panels as HCO3 or bicarbonate.

Where might you see it?

On arterial/venous blood gas reports and clinical chemistry panels.

When might you encounter it?

During renal tubular acidosis follow-up, or when the team adjusts individualized alkali support — not as a mandatory test in every situation.

Where on this site?

Treatment — RTA · Family toolkit · Clinical quick reference

Practical example

A family seeing “HCO3 = 15” can ask how that number fits the current RTA plan. This site explains the concept; it does not set universal dose targets.

Potassium
K
Related page

Lab Kidney Clinic Treatment

What is it?

An electrolyte important for muscle and heart function; often monitored in RTA care plans.

Where might you see it?

On serum electrolyte panels and sometimes in home logs requested by clinic teams.

When might you encounter it?

When reviewing labs, muscle/heart symptoms the team links to electrolytes, or adjusting supportive therapy.

Where on this site?

Treatment — RTA · Family toolkit

Practical example

Low potassium may enter an RTA discussion; this site does not interpret a single number or suggest unsupervised replacement.

Autosomal recessive
Related page

Genetics Clinical reports

What is it?

An inheritance pattern that usually requires two pathogenic gene copies for disease expression.

Where might you see it?

In genetic counseling letters, sequencing reports, and disease explainers.

When might you encounter it?

When discussing recurrence risk or reading “AR inheritance” in a report.

Where on this site?

About the disease · CA II in Saudi Arabia · For families

Practical example

“Autosomal recessive” usually means both alleles are affected; family-specific risks belong in genetics counseling.

Biallelic
Related page

Genetics Clinical reports

What is it?

Pathogenic changes affecting both alleles of the gene.

Where might you see it?

In molecular genetics reports and genetic diagnosis summaries.

When might you encounter it?

When reading results such as “biallelic pathogenic variants in CA2”.

Where on this site?

About the disease · Variant pathway

Practical example

Biallelic CA2 variants support a genetic diagnosis of CA II deficiency when clinical features fit — final interpretation rests with the reporting laboratory and clinical genetics.

Variant
Related page

Genetics Research Clinical reports

What is it?

A DNA sequence change; not every change causes disease, and pathogenicity needs expert interpretation.

Where might you see it?

In NGS/CA2 sequencing reports, databases, and research discussions.

When might you encounter it?

When receiving a genetics result or reading papers about CA2 variants.

Where on this site?

Variant pathway · Variant-effect types · Library

Practical example

A “VUS” (variant of uncertain significance) is not the same as a pathogenic call; this site does not reclassify individual variants outside the laboratory report.

Splice-site variant
Related page

Genetics Research

What is it?

A variant affecting RNA splicing signals, which can change production of functional protein.

Where might you see it?

In genetics reports naming splice positions such as c.232+1G>A or related changes.

When might you encounter it?

When discussing variants reported in published cohorts — without assuming identical severity for every person.

Where on this site?

Splice-variant context · Variant-effect types · Saudi Arabia

Practical example

A splice variant reported in Arabic-patient literature is not labeled here as a “Saudi mutation,” and phenotype can still vary.

Frameshift
Related page

Genetics Research

What is it?

An insertion or deletion that shifts the reading frame and may cause major loss of function, depending on molecular context.

Where might you see it?

In molecular-effect descriptions within reports or papers.

When might you encounter it?

When classifying molecular lesion type in genotype–phenotype discussions.

Where on this site?

Variant-effect types · Genotype–phenotype correlation

Practical example

Calling a change a frameshift explains a possible loss-of-function mechanism; it does not by itself prescribe a treatment plan.

Hypomorphic
Related page

Genetics Research

What is it?

A variant that reduces enzyme function without necessarily abolishing it (reduced residual activity).

Where might you see it?

In molecular papers and discussions linking variant class to severity.

When might you encounter it?

When comparing severe loss-of-function alleles with residual-function examples from the literature.

Where on this site?

H107Y spotlight · Residual activity

Practical example

Roth et al. (PMID 1542674) described H107Y with detectable but greatly reduced activity — a research example, not a routine clinic assay for every patient.

Residual activity
Related page

Genetics Research Lab

What is it?

How much CA II enzyme activity remains after a genetic change; important in the literature and not routinely available in every clinic.

Where might you see it?

More often in molecular/lab studies than in day-to-day clinic printouts.

When might you encounter it?

When interpreting why some published variants associate with milder features — without over-generalizing to one person.

Where on this site?

Variant pathway · H107Y · Research gaps

Practical example

Published residual activity for one variant does not mean every clinic can measure the same activity for every patient today.

Genotype
Related page

Genetics Research

What is it?

The person’s genetic variant configuration (what is present in the gene).

Where might you see it?

In sequencing reports, family studies, and paper tables.

When might you encounter it?

When comparing people with different variants or reading genotype–phenotype sections.

Where on this site?

Clinical heterogeneity · Variant pathway

Practical example

The same clinical label “CA II deficiency” can map to different genotypes; genotype is part of the picture, not the whole care decision.

Phenotype
Related page

Clinic Clinical reports Research

What is it?

Observable clinical and laboratory features (what is seen in the patient).

Where might you see it?

In clinical summaries, case tables, and bone/kidney/neurologic follow-up.

When might you encounter it?

When describing severity, complications, or differences among relatives.

Where on this site?

About the disease · Treatment · What we know

Practical example

A severe skeletal phenotype may coexist with variable renal acidosis; this site emphasizes heterogeneity rather than one mandatory picture.

Genotype–phenotype correlation
Related page

Genetics Research Treatment

What is it?

Efforts to relate variant type to clinical severity or residual activity — observed associations, not deterministic rules for individuals, and not mutation-specific drug selection.

Where might you see it?

In genetics research, literature reviews, and treatment sections on heterogeneity.

When might you encounter it?

When comparing variant class with disease severity, or reading the H107Y example and related published variants.

Where on this site?

Heterogeneity · H107Y · What we know · Research gaps

Practical example

Example: H107Y in PMID 1542674 had residual activity and relatively milder features in a compound-heterozygous context — supporting correlation without proving mutation-guided prescribing.

Osteopetrosis
Related page

Bone Imaging Clinic

What is it?

Increased bone density that can still involve fragility or cranial complications despite a denser radiographic appearance.

Where might you see it?

In radiology reports, bone summaries, and genetic osteopetrosis literature.

When might you encounter it?

When discussing fractures, cranial nerve compromise, or selected severe cases where HSCT is considered.

Where on this site?

About the disease · HSCT · Treatment

Practical example

Osteopetrosis in CA II deficiency does not automatically mean therapies used in other osteopetrosis types are appropriate; the treatment page warns against that generalization.

Cerebral calcification
Related page

Neurology Imaging Clinical reports

What is it?

Calcium deposits in the brain reported on some imaging studies; described in many published CA II cases, not universal at every age.

Where might you see it?

In CT/MRI reports or neurology summaries.

When might you encounter it?

When following neurologic features or comparing calcification trajectory across published follow-up.

Where on this site?

About the disease · What we know · Research gaps

Practical example

Later calcification after transplant in some published HSCT contexts shows neurologic pathways may continue — without generalizing to every patient.

Hematopoietic Stem Cell Transplantation
HSCT
Related page

Transplant Bone Treatment Research

What is it?

Transplant of blood-forming stem cells; discussed by specialists in selected situations, not standard care for every person with CA II deficiency.

Where might you see it?

In the scientific literature, case reports, and transplant-center discussions for selected severe skeletal disease.

When might you encounter it?

When weighing possible skeletal benefit against persistence of RTA or neurologic features; decisions are individualized and multidisciplinary.

Where on this site?

Treatment — HSCT · Why HSCT does not fix everything · Research gaps · Quick reference

Practical example

Reports such as PMID 11264157 and PMID 38655726 describe limited cases: skeletal disease may improve while RTA persists — not a general protocol.

Supportive treatment
Related page

Treatment Kidney Clinic

What is it?

Care that supports physiology and complications (such as acid–base and electrolyte management) without claiming to cure the genetic cause.

Where might you see it?

In clinic plans, treatment pages, and family organizing tools for follow-up.

When might you encounter it?

In most day-to-day care pathways for CA II deficiency, where individualized support is the published mainstay.

Where on this site?

Supportive care · Family toolkit · For families

Practical example

Alkali support is individualized; this site explains the idea and does not publish general doses.

Clinical management
Related page

Clinic Treatment

What is it?

The follow-up and interventions set by the treating team for an individual — not a mandatory universal algorithm for this rare disease.

Where might you see it?

In multidisciplinary clinic summaries and this site’s treatment page.

When might you encounter it?

When coordinating kidney, bone, genetics, and neurology visits, or discussing limited-evidence options.

Where on this site?

Treatment & clinical management · For clinicians · Quick reference

Practical example

On this site, “clinical management” means a framework for understanding and follow-up — not a printable order set.